COLUMBUS, Ohio, Dec. 18, 2023 /PRNewswire/ -- Andelyn Biosciences, Inc., a pioneering and patient-focused cell and gene therapy Contract Development and Manufacturing Organization (CDMO), announced ...
CLN2, a form of Batten disease caused by TPP1 protein deficiency, is a pediatric neurodegenerative disorder with an estimated incidence of 0.5 per 100,000 live births. Most affected children begin ...